Asparaginase-Phage P22 Nanoreactors: Toward a Biobetter Development for Acute Lymphoblastic Leukemia Treatment


Por: Diaz-Barriga, Cristina, Villanueva-Flores, Francisca, Quester, Katrin, Zarate-Romero, Andres, Cadena-Nava, Ruben Dario, Huerta-Saquero, Alejandro

Publicada: 1 may 2021
Categoría: Pharmaceutical science

Resumen:
Asparaginase (ASNase) is a biopharmaceutical for Acute Lymphoblastic Leukemia (ALL) treatment. However, it shows undesirable side effects such as short lifetimes, susceptibility to proteases, and immunogenicity. Here, ASNase encapsidation was genetically directed in bacteriophage P22-based virus-like particles (VLPs) (ASNase-P22 nanoreactors) as a strategy to overcome these challenges. ASNase-P22 was composed of 58.4 +/- 7.9% of coat protein and 41.6 +/- 8.1% of tetrameric ASNase. Km and Kcat values of ASNase-P22 were 15- and 2-fold higher than those obtained for the free enzyme, respectively. Resulting Kcat/Km value was 2.19 x 10(5) M-1 s(-1). ASNase-P22 showed an aggregation of 60% of the volume sample when incubated at 37 degrees C for 12 days. In comparison, commercial asparaginase was completely aggregated under the same conditions. ASNase-P22 was stable for up to 24 h at 37 degrees C, independent of the presence of human blood serum (HBS) or whether ASNase-P22 nanoreactors were uncoated or PEGylated. Finally, we found that ASNase-P22 caused cytotoxicity in the leukemic cell line MOLT-4 in a concentration dependent manner. To our knowledge, this is the first work where ASNase is encapsulated inside of VLPs, as a promising alternative to fight ALL.

Filiaciones:
Diaz-Barriga, Cristina:
 Centro de Nanociencias y Nanotecnología, Universidad Nacional Autónoma de México, Km. 107 Carretera Tijuana-Ensenada, Ensenada, 22860, Mexico

Villanueva-Flores, Francisca:
 Centro de Nanociencias y Nanotecnología, Universidad Nacional Autónoma de México, Km. 107 Carretera Tijuana-Ensenada, Ensenada, 22860, Mexico

Quester, Katrin:
 Centro de Nanociencias y Nanotecnología, Universidad Nacional Autónoma de México, Km. 107 Carretera Tijuana-Ensenada, Ensenada, 22860, Mexico

Zarate-Romero, Andres:
 Centro de Nanociencias y Nanotecnología, Universidad Nacional Autónoma de México, Km. 107 Carretera Tijuana-Ensenada, Ensenada, 22860, Mexico

Cadena-Nava, Ruben Dario:
 Centro de Nanociencias y Nanotecnología, Universidad Nacional Autónoma de México, Km. 107 Carretera Tijuana-Ensenada, Ensenada, 22860, Mexico

Huerta-Saquero, Alejandro:
 Centro de Nanociencias y Nanotecnología, Universidad Nacional Autónoma de México, Km. 107 Carretera Tijuana-Ensenada, Ensenada, 22860, Mexico
ISSN: 19994923





Pharmaceutics
Editorial
MDPI AG, ST ALBAN-ANLAGE 66, CH-4052 BASEL, SWITZERLAND, Suiza
Tipo de documento: Article
Volumen: 13 Número: 5
Páginas:
WOS Id: 000662433000001
ID de PubMed: 33922106
imagen Gold, Green Published, All Open Access; Gold

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