Expressed gene fusions as frequent drivers of poor outcomes in hormone receptor–positive breast cancer


Por: Matissek K.J., Onozato M.L., Sun S., Zheng Z., Schultz A., Lee J., Patel K., Jerevall P.-L., Saladi S.V., Macleay A., Tavallai M., Badovinac-Crnjevic T., Barrios C., BeÅŸe N., Chan A., Chavarri-Guerra Y., Debiasi M., Demirdogen E., Egeli U., Gokgoz S., Gomez H., Liedke P., Tasdelen I., Tolunay S., Werutsky G., Louis J.S., Horick N., Finkelstein D.M., Le L.P., Bardia A., Goss P.E., Sgroi D.C., Iafrate A.J., Ellisen L.W.

Publicada: 1 ene 2018
Categoría: Oncology

Resumen:
We sought to uncover genetic drivers of hormone receptor–positive (HR +) breast cancer, using a targeted next-generation sequencing approach for detecting expressed gene rearrangements without prior knowledge of the fusion partners. We identifi ed intergenic fusions involving driver genes, including PIK3CA, AKT3, RAF1, and ESR1, in 14% (24/173) of unselected patients with advanced HR + breast cancer. FISH confi rmed the corresponding chromosomal rearrangements in both primary and metastatic tumors. Expression of novel kinase fusions in nontransformed cells deregulates phosphoprotein signaling, cell proliferation, and survival in threedimensional culture, whereas expression in HR + breast cancer models modulates estrogen-dependent growth and confers hormonal therapy resistance in vitro and in vivo. Strikingly, shorter overall survival was observed in patients with rearrangement-positive versus rearrangement-negative tumors. Correspondingly, fusions were uncommon (<5%) among 300 patients presenting with primary HR + breast cancer. Collectively, our fi ndings identify expressed gene fusions as frequent and potentially actionable drivers in HR + breast cancer. SIGNIFICANCE: By using a powerful clinical molecular diagnostic assay, we identifi ed expressed intergenic fusions as frequent contributors to treatment resistance and poor survival in advanced HR + breast cancer. The prevalence and biological and prognostic signifi cance of these alterations suggests that their detection may alter clinical management and bring to light new therapeutic opportunities. © 2018 American Association for Cancer Research.

Filiaciones:
Matissek K.J.:
 Massachusetts General Hospital Cancer Center, Boston, MA, United States

 Harvard Medical School, Boston, MA, United States

Onozato M.L.:
 Department of Pathology, Massachusetts General Hospital, Boston, MA, United States

Sun S.:
 Massachusetts General Hospital Cancer Center, Boston, MA, United States

 Harvard Medical School, Boston, MA, United States

Zheng Z.:
 Harvard Medical School, Boston, MA, United States

 Department of Pathology, Massachusetts General Hospital, Boston, MA, United States

 Department of Medical Epidemiology and Biostatistics, Karolinska Institutet, Stockholm, Sweden

Schultz A.:
 Massachusetts General Hospital Cancer Center, Boston, MA, United States

Lee J.:
 Department of Pathology, Massachusetts General Hospital, Boston, MA, United States

Patel K.:
 Massachusetts General Hospital Cancer Center, Boston, MA, United States

Jerevall P.-L.:
 Harvard Medical School, Boston, MA, United States

 Department of Pathology, Massachusetts General Hospital, Boston, MA, United States

Saladi S.V.:
 Massachusetts General Hospital Cancer Center, Boston, MA, United States

 Harvard Medical School, Boston, MA, United States

Macleay A.:
 Department of Pathology, Massachusetts General Hospital, Boston, MA, United States

Tavallai M.:
 Massachusetts General Hospital Cancer Center, Boston, MA, United States

 Harvard Medical School, Boston, MA, United States

Badovinac-Crnjevic T.:
 University Hospital Zagreb, Zagreb, Croatia

Barrios C.:
 Latin America Cooperative Oncology Group (LACOG) and Pontificia Universidade Catolica do Rio Grande do Sul (PUCRS), Porto Alegre, Brazil

Chan A.:
 Mount Hospital, Perth, Australia

Chavarri-Guerra Y.:
 Instituto Nacional de Ciencias Medicas y Nutrición Salvador Zubiran, D.F., México City, Mexico

Debiasi M.:
 Latin America Cooperative Oncology Group (LACOG) and Pontificia Universidade Catolica do Rio Grande do Sul (PUCRS), Porto Alegre, Brazil

Demirdogen E.:
 Departments of Medical Biology, General Surgery, Pathology of Medical Faculty of Uludag University, Bursa, Turkey

Egeli U.:
 Departments of Medical Biology, General Surgery, Pathology of Medical Faculty of Uludag University, Bursa, Turkey

Gokgoz S.:
 Departments of Medical Biology, General Surgery, Pathology of Medical Faculty of Uludag University, Bursa, Turkey

Gomez H.:
 Instituto Nacional de Enfermedades Neoplasicas, Lima, Peru

Liedke P.:
 Latin America Cooperative Oncology Group (LACOG) and Pontificia Universidade Catolica do Rio Grande do Sul (PUCRS), Porto Alegre, Brazil

Tasdelen I.:
 Departments of Medical Biology, General Surgery, Pathology of Medical Faculty of Uludag University, Bursa, Turkey

Tolunay S.:
 Departments of Medical Biology, General Surgery, Pathology of Medical Faculty of Uludag University, Bursa, Turkey

Werutsky G.:
 Latin America Cooperative Oncology Group (LACOG) and Pontificia Universidade Catolica do Rio Grande do Sul (PUCRS), Porto Alegre, Brazil

Louis J.S.:
 Massachusetts General Hospital Cancer Center, Boston, MA, United States

Horick N.:
 Biostatistics Center, Massachusetts General Hospital, Boston, MA, United States

Finkelstein D.M.:
 Harvard Medical School, Boston, MA, United States

 Biostatistics Center, Massachusetts General Hospital, Boston, MA, United States

Le L.P.:
 Harvard Medical School, Boston, MA, United States

 Department of Pathology, Massachusetts General Hospital, Boston, MA, United States

Bardia A.:
 Massachusetts General Hospital Cancer Center, Boston, MA, United States

 Harvard Medical School, Boston, MA, United States

Goss P.E.:
 Massachusetts General Hospital Cancer Center, Boston, MA, United States

 Harvard Medical School, Boston, MA, United States

Sgroi D.C.:
 Harvard Medical School, Boston, MA, United States

 Department of Pathology, Massachusetts General Hospital, Boston, MA, United States

Iafrate A.J.:
 Harvard Medical School, Boston, MA, United States

 Department of Pathology, Massachusetts General Hospital, Boston, MA, United States

Ellisen L.W.:
 Massachusetts General Hospital Cancer Center, Boston, MA, United States

 Harvard Medical School, Boston, MA, United States

Department of Radiation Oncology, Acibadem Breast Research Institute, Istanbul, Turkey
ISSN: 21598274
Editorial
American Association for Cancer Research Inc., Estados Unidos America
Tipo de documento: Article
Volumen: 8 Número: 3
Páginas: 336-353
WOS Id: 000426997500023
ID de PubMed: 29242214
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